Using yeast cells engineered to express variants that cause ultra-rare metabolic diseases, a collaboration between Perlara, UCSF and motivated families has yielded actionable repurposing hits.
Yeast avatars for drug repurposing
Using yeast cells engineered to express variants that cause ultra-rare metabolic diseases, a collaboration between Perlara, UCSF and motivated families has yielded actionable repurposing hits.