Using yeast cells engineered to express variants that cause ultra-rare metabolic diseases, a collaboration between Perlara, UCSF and motivated families has yielded actionable repurposing hits.
Yeast avatars for drug repurposing
Yeast avatars for drug repurposing
Yeast avatars for drug repurposing
Using yeast cells engineered to express variants that cause ultra-rare metabolic diseases, a collaboration between Perlara, UCSF and motivated families has yielded actionable repurposing hits.