Using worm and fly avatars, we identified three hits with a shared pharmacophore that appears to target another CDG gene. We're testing a metabolic rebalancing hypothesis in patient fibroblasts next.
GMPPA-CDG Cure Odyssey
GMPPA-CDG Cure Odyssey
GMPPA-CDG Cure Odyssey
Using worm and fly avatars, we identified three hits with a shared pharmacophore that appears to target another CDG gene. We're testing a metabolic rebalancing hypothesis in patient fibroblasts next.