The 6th Cure Roadmap was commissioned by the Malan Syndrome Foundation. We made the case for drug repurposing and gene up-regulating ASOs, and sparked a collaboration to derive iPSCs from urine.
NFIX Cure Roadmap
The 6th Cure Roadmap was commissioned by the Malan Syndrome Foundation. We made the case for drug repurposing and gene up-regulating ASOs, and sparked a collaboration to derive iPSCs from urine.